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Efficacy and safety of thalidomide in children with monogenic autoinflammatory diseases: a single-center, real-world-evidence study

BACKGROUND: Monogenic autoinflammatory diseases (AIDs) are rare inflammatory diseases caused by genetic variants. The pathogenesis is complex and treatment options are limited. This study aimed to describe the safety and efficacy of thalidomide in the treatment of monogenic AIDs. METHODS: This was a...

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Detalles Bibliográficos
Autores principales:	Zhang, Caihui, Yu, Zhongxun, Gao, Sihao, Ma, Mingsheng, Gou, Lijuan, Wang, Changyan, Wang, Lin, Li, Ji, Zhong, Linqing, Zhou, Yu, Wang, Wei, Song, Hongmei
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2023
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10583446/ https://www.ncbi.nlm.nih.gov/pubmed/37848905 http://dx.doi.org/10.1186/s12969-023-00881-0

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