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Efficacy and safety of thalidomide in children with monogenic autoinflammatory diseases: a single-center, real-world-evidence study
BACKGROUND: Monogenic autoinflammatory diseases (AIDs) are rare inflammatory diseases caused by genetic variants. The pathogenesis is complex and treatment options are limited. This study aimed to describe the safety and efficacy of thalidomide in the treatment of monogenic AIDs. METHODS: This was a...
Autores principales: | Zhang, Caihui, Yu, Zhongxun, Gao, Sihao, Ma, Mingsheng, Gou, Lijuan, Wang, Changyan, Wang, Lin, Li, Ji, Zhong, Linqing, Zhou, Yu, Wang, Wei, Song, Hongmei |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BioMed Central
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10583446/ https://www.ncbi.nlm.nih.gov/pubmed/37848905 http://dx.doi.org/10.1186/s12969-023-00881-0 |
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