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Infrastructural considerations of implementing gene therapy for hemophilia in the Nordic context

BACKGROUND: Despite improvements in hemophilia care, challenges remain, including treatment burden and impaired quality of life. Gene therapy may overcome these. However, its introduction presents a challenge. OBJECTIVES: To outline a function-based gene therapy working model describing critical mil...

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Detalles Bibliográficos
Autores principales:	Astermark, Jan, Baghaei, Fariba, Strandberg, Karin, Toplican, Petra Gabric, Birkedal, Maj Friberg, Grahn, Emma Engman, Hansson, Charlotta, Kampmann, Peter, Lehtinen, Anna-Elina, Täckström, Kinga, Holme, Pål Andre, Magnusson, Maria
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	SAGE Publications 2023
Materias:	Original Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10583513/ https://www.ncbi.nlm.nih.gov/pubmed/37859645 http://dx.doi.org/10.1177/20406207231202306

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