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MicroRNA Profile, Putative Diagnostic Biomarkers and RNA-Based Therapies in the Inherited Lipid Storage Disease Niemann-Pick Type C

Lipids are essential for cellular function and are tightly controlled at the transcriptional and post-transcriptional levels. Dysregulation of these pathways is associated with vascular diseases, diabetes, cancer, and several inherited metabolic disorders. MicroRNAs (miRNAs), in particular, are a fa...

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Detalles Bibliográficos
Autores principales:	Encarnação, Marisa, David, Hugo, Coutinho, Maria Francisca, Moreira, Luciana, Alves, Sandra
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	MDPI 2023
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10604387/ https://www.ncbi.nlm.nih.gov/pubmed/37892989 http://dx.doi.org/10.3390/biomedicines11102615

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