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Advances in gene therapy for inborn errors of immunity

PURPOSE OF REVIEW: Provide an overview of the landmark accomplishments and state of the art of gene therapy for inborn errors of immunity (IEI). RECENT FINDINGS: Three decades after the first clinical application of gene therapy for IEI, there is one market authorized product available, while for se...

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Detalles Bibliográficos
Autores principales:	Ott de Bruin, Lisa M., Lankester, Arjan C., Staal, Frank J.T.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2023
Materias:	PRIMARY IMMUNE DEFICIENCY DISEASE: Edited by Francesco Cinetto and Virgil Dalm
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10621649/ https://www.ncbi.nlm.nih.gov/pubmed/37846903 http://dx.doi.org/10.1097/ACI.0000000000000952

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