Twice-Weekly Outpatient Rehabilitation Intervention for Young Children With Spinal Muscular Atrophy Treated With Genetic-Based Therapies: Protocol for a Feasibility Study

BACKGROUND: Spinal muscular atrophy (SMA) is a progressive neuromuscular disorder that causes muscle weakness and is the leading genetic cause of infant mortality worldwide. While no definitive cure exists, the approval of 3 genetic-based therapies in Canada since 2018 has led to significant improve...

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Detalles Bibliográficos
Autores principales: Ippolito, Christina, Canthiya, Lathushikka, Floreani, Amanda, Luckhart, Kathleen, Hoffman, Andrea, McAdam, Laura
Formato: Online Artículo Texto
Lenguaje:English
Publicado: JMIR Publications 2023
Materias:
Protocol
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10654912/
https://www.ncbi.nlm.nih.gov/pubmed/37917140
http://dx.doi.org/10.2196/46363

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