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Safety and Efficacy of Adeno-Associated Viral Gene Therapy in Patients With Retinal Degeneration: A Systematic Review and Meta-Analysis

PURPOSE: This systematic review evaluates the safety and efficacy of ocular gene therapy using adeno-associated virus (AAV). METHODS: MEDLINE, Embase, Cochrane Central Register of Controlled Trials, and ClinicalTrials.gov were searched systematically for controlled or non-controlled interventional g...

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Detalles Bibliográficos
Autores principales:	Sobh, Mohamad, Lagali, Pamela S., Ghiasi, Maryam, Montroy, Joshua, Dollin, Michael, Hurley, Bernard, Leonard, Brian C., Dimopoulos, Ioannis, Lafreniere, Mackenzie, Fergusson, Dean A., Lalu, Manoj M., Tsilfidis, Catherine
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	The Association for Research in Vision and Ophthalmology 2023
Materias:	Retina
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10668613/ https://www.ncbi.nlm.nih.gov/pubmed/37982768 http://dx.doi.org/10.1167/tvst.12.11.24

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