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Nusinersen for Spinal Muscular Atrophy Type I with Chronic Respiratory Failure: A Retrospective Study in South Korea

PURPOSE: To analyze the efficacy and safety of nusinersen in patients with spinal muscular atrophy (SMA) type I with chronic respiratory failure. MATERIALS AND METHODS: We retrospectively reviewed seven patients diagnosed with SMA type I and chronic respiratory failure who were on permanent ventilat...

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Detalles Bibliográficos
Autores principales:	Shin, Hui Jin, Na, Ji-Hoon, Lee, Hyunjoo, Lee, Young-Mock
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Yonsei University College of Medicine 2023
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10681826/ https://www.ncbi.nlm.nih.gov/pubmed/37992742 http://dx.doi.org/10.3349/ymj.2023.0080

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