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Real-world evidence of eteplirsen treatment effects in patients with Duchenne muscular dystrophy in the USA
AIM: To evaluate treatment effects of eteplirsen among patients with Duchenne muscular dystrophy. METHODS: Using real-world claims and electronic medical record data, this retrospective comparative analysis assessed eteplirsen-treated and control cohorts matched by age, disease progression state, an...
Autores principales: | Iff, Joel, Zhong, Yi, Tuttle, Edward, Gupta, Deepshekhar, Paul, Xander, Henricson, Erik |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Becaris Publishing Ltd
2023
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10690424/ https://www.ncbi.nlm.nih.gov/pubmed/37610303 http://dx.doi.org/10.57264/cer-2023-0086 |
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