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A Look to Future Directions in Gene Therapy Research for Monogenic Diseases
The concept of gene therapy has long appealed to biomedical researchers and clinicians because it promised to treat certain diseases at their origins. In the last several years, there have been several trials in which patients have benefited from gene therapy protocols. This progress, however, has r...
Autores principales: | Porteus, Matthew H, Connelly, Jon P, Pruett, Shondra M |
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Formato: | Texto |
Lenguaje: | English |
Publicado: |
Public Library of Science
2006
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC1584267/ https://www.ncbi.nlm.nih.gov/pubmed/17009872 http://dx.doi.org/10.1371/journal.pgen.0020133 |
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