Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy

BACKGROUND: Antisense-mediated exon skipping is currently one of the most promising therapeutic approaches for Duchenne muscular dystrophy (DMD). Using antisense oligonucleotides (AONs) targeting specific exons the DMD reading frame is restored and partially functional dystrophins are produced. Foll...

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Detalles Bibliográficos
Autores principales: Aartsma-Rus, Annemieke, Janson, Anneke AM, van Ommen, Gert-Jan B, van Deutekom, Judith CT
Formato: Texto
Lenguaje:English
Publicado: BioMed Central 2007
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC1931584/
https://www.ncbi.nlm.nih.gov/pubmed/17612397
http://dx.doi.org/10.1186/1471-2350-8-43

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