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Short-Term Efficacy of Enzyme Replacement Therapy in Korean Patients with Fabry Disease

Fabrazyme has been widely used for treatment of Fabry disease since its approval by the U.S. Food and Drug Administration in 2003. This study was undertaken to assess the short-term efficacy and safety of enzyme replacement therapy (ERT) for Fabry disease in Korea. Eight male patients and three fema...

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Detalles Bibliográficos
Autores principales:	Choi, Jin-Ho, Cho, Young Mi, Suh, Kwang-Sun, Yoon, Hye-Ran, Kim, Gu-Hwan, Kim, Sung-Su, Ko, Jung Min, Lee, Joo Hoon, Park, Young Seo, Yoo, Han-Wook
Formato:	Texto
Lenguaje:	English
Publicado:	The Korean Academy of Medical Sciences 2008
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC2526436/ https://www.ncbi.nlm.nih.gov/pubmed/18437007 http://dx.doi.org/10.3346/jkms.2008.23.2.243

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