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Gene Therapy in Thalassemia and Hemoglobinopathies

Sickle cell disease (SCD) and ß-thalassemia represent the most common hemoglobinopathies caused, respectively, by the alteration of structural features or deficient production of the ß-chain of the Hb molecule. Other hemoglobinopathies are characterized by different mutations in the α- or ß-globin g...

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Detalles Bibliográficos
Autores principales:	Breda, Laura, Gambari, Roberto, Rivella, Stefano
Formato:	Texto
Lenguaje:	English
Publicado:	Università Cattolica del Sacro Cuore 2009
Materias:	Review Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3033156/ https://www.ncbi.nlm.nih.gov/pubmed/21415990 http://dx.doi.org/10.4084/MJHID.2009.008

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