Cargando…

In vivo genome editing restores hemostasis in a mouse model of hemophilia

Detalles Bibliográficos
Autores principales:	Li, Hojun, Haurigot, Virginia, Doyon, Yannick, Li, Tianjian, Wong, Sunnie Y., Bhagwat, Anand S., Malani, Nirav, Anguela, Xavier M., Sharma, Rajiv, Ivanciu, Lacramiora, Murphy, Samuel L., Finn, Jonathan D., Khazi, Fayaz R., Zhou, Shangzhen, Paschon, David E., Rebar, Edward J., Bushman, Frederic D., Gregory, Philip D., Holmes, Michael C., High, Katherine A.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	2011
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3152293/ https://www.ncbi.nlm.nih.gov/pubmed/21706032 http://dx.doi.org/10.1038/nature10177

Ejemplares similares

Safety of AAV Factor IX Peripheral Transvenular Gene Delivery to Muscle in Hemophilia B Dogs
por: Haurigot, Virginia, et al.
Publicado: (2010)

Successful Phenotype Improvement following Gene Therapy for Severe Hemophilia A in Privately Owned Dogs
por: Callan, Mary Beth, et al.
Publicado: (2016)

Management of perioperative hemostasis in a severe hemophilia A patient with inhibitors on emicizumab using global hemostasis assays
por: Kizilocak, Hande, et al.
Publicado: (2019)

RNAi targeting heparin cofactor II promotes hemostasis in hemophilia A
por: Lin, Wen-yi, et al.
Publicado: (2021)

Oracle or false prophet? Can we predict AAV efficacy based on preexisting antibody titers?
por: Anguela, Xavier M., et al.
Publicado: (2019)

Assessment of acquired hemophilia patient demographics in the United States: the Hemostasis and Thrombosis Research Society Registry
por: Kessler, Craig M., et al.
Publicado: (2016)

Phosphatidylserine positive microparticles improve hemostasis in in-vitro hemophilia A plasma models
por: Zong, Yanan, et al.
Publicado: (2020)

Pharmacological Modulation of Humoral Immunity in a Nonhuman Primate Model of AAV Gene Transfer for Hemophilia B
por: Mingozzi, Federico, et al.
Publicado: (2012)

Use of recombinant activated factor VII for acute bleeding episodes in acquired hemophilia: final analysis from the Hemostasis and Thrombosis Research Society Registry acquired hemophilia study
por: Ma, Alice D., et al.
Publicado: (2016)

Microfluidic hemophilia models using blood from healthy donors
por: Yu, Xinren, et al.
Publicado: (2019)

Platelet-Targeted FVIII Gene Therapy Restores Hemostasis and Induces Immune Tolerance for Hemophilia A
por: Cai, Yuanhua, et al.
Publicado: (2020)

Recombinant factor IX Fc for major surgery in hemophilia B: factor IX plasma activity levels and effective hemostasis
por: Shapiro, Amy D., et al.
Publicado: (2023)

Preclinical assessment of an optimized AAV-FVIII vector in mice and non-human primates for the treatment of hemophilia A
por: Elkouby, Liron, et al.
Publicado: (2021)

Acquired hemophilia A that required surgical hemostasis of hematomas occupying oral cavity: a case report
por: Maeda, Keigo, et al.
Publicado: (2021)

HRP-2 determines HIV-1 integration site selection in LEDGF/p75 depleted cells
por: Schrijvers, Rik, et al.
Publicado: (2012)

A Retrospective Analysis of the American Thrombosis and Hemostasis Network Dataset Describing Outcomes of Dental Extractions in Persons with Hemophilia
por: Messenger, Heather, et al.
Publicado: (2023)

Cellular Localization and Characterization of Cytosolic Binding Partners for Gla Domain-containing Proteins PRRG4 and PRRG2
por: Yazicioglu, Mustafa N., et al.
Publicado: (2013)

Prevention and Reversal of Antibody Responses Against Factor IX in Gene Therapy for Hemophilia B
por: Nayak, Sushrusha, et al.
Publicado: (2011)

Structural and sequencing analysis of local target DNA recognition by MLV integrase
por: Aiyer, Sriram, et al.
Publicado: (2015)

CRISPR-Cas9-Mediated In Vivo Gene Integration at the Albumin Locus Recovers Hemostasis in Neonatal and Adult Hemophilia B Mice
por: Wang, Qingnan, et al.
Publicado: (2020)

MG1113, a specific anti–tissue factor pathway inhibitor antibody, rebalances the coagulation system and promotes hemostasis in hemophilia
por: Kwak, Heechun, et al.
Publicado: (2020)

Hemostasis Strategies and Recent Advances in Nanomaterials for Hemostasis
por: Du, Jian, et al.
Publicado: (2023)

Hemostasis in Overt and Subclinical Hyperthyroidism
por: Ordookhani, Arash, et al.
Publicado: (2017)

Low-dose AAV-CRISPR-mediated liver-specific knock-in restored hemostasis in neonatal hemophilia B mice with subtle antibody response
por: He, Xiangjun, et al.
Publicado: (2022)

Hemostasis in Hypothyroidism and Autoimmune Thyroid Disorders
por: Ordookhani, Arash, et al.
Publicado: (2017)

The History of Hemostasis
por: Wies, C. H.
Publicado: (1929)

Hemostasis and ageing
por: Mari, Daniela, et al.
Publicado: (2008)

Hematology and Hemostasis
por: Finke, Jürgen, et al.
Publicado: (2008)

The History of Hemostasis
por: Klopp, Edward J.
Publicado: (1930)

The History of Hemostasis
por: Harvey, Samuel C.
Publicado: (1929)

Hibernation and hemostasis
por: De Vrij, Edwin L., et al.
Publicado: (2023)

Correction of the coagulation defect in hemophilia using a factor Xa variant with novel engineered protease function
por: Ivanciu, Lacramioara, et al.
Publicado: (2011)

Hemostasis, bleeding and thrombosis in liver disease
por: Flores, Brisas, et al.
Publicado: (2017)

Bromodomain and extra-terminal (BET) proteins target Moloney murine leukemia virus integration to transcription start sites
por: De Riick, Jan, et al.
Publicado: (2013)

Treatment adherence in hemophilia
por: Thornburg, Courtney D, et al.
Publicado: (2017)

Hemostasis-On-a-Chip: Impedance Spectroscopy Meets Microfluidics for Hemostasis Evaluation
por: Karimi, Shadi, et al.
Publicado: (2019)

Comparative Analysis of the Recently Discovered hAT Transposon TcBuster in Human Cells
por: Woodard, Lauren E., et al.
Publicado: (2012)

Hemophilia Burden of Disease: A Systematic Review of the Cost-Utility Literature for Hemophilia
por: Thorat, Teja, et al.
Publicado: (2018)

Influence of antidepressants on hemostasis
por: Halperin, Demian, et al.
Publicado: (2007)

Hemostasis with the Ultrasonic Scalpel
por: Crispi, Claudio Peixoto, et al.
Publicado: (2018)

Cannot write session to /tmp/vufind_sessions/sess_jkdljnig5v0fmom3f1n0chor0t