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Stem cell-based therapy for α(1)-antitrypsin deficiency

Human induced pluripotent stem cells offer the possibility of generating unlimited quantities of cells for autologous transplantation. By correcting the genetic defect underlying Z-allele α(1)-antitrypsin deficiency, we recently provided the first proof of principle for application of human induced...

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Detalles Bibliográficos
Autores principales:	Rashid, S Tamir, Lomas, David A
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2012
Materias:	Commentary
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3340548/ https://www.ncbi.nlm.nih.gov/pubmed/22340671 http://dx.doi.org/10.1186/scrt95

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