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Gene therapy in animal models of autosomal dominant retinitis pigmentosa
Gene therapy for dominantly inherited genetic disease is more difficult than gene-based therapy for recessive disorders, which can be treated with gene supplementation. Treatment of dominant disease may require gene supplementation partnered with suppression of the expression of the mutant gene eith...
Autores principales: | Rossmiller, Brian, Mao, Haoyu, Lewin, Alfred S. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Molecular Vision
2012
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3472929/ https://www.ncbi.nlm.nih.gov/pubmed/23077406 |
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