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Transcription factor EB (TFEB) is a new therapeutic target for Pompe disease

A recently proposed therapeutic approach for lysosomal storage disorders (LSDs) relies upon the ability of transcription factor EB (TFEB) to stimulate autophagy and induce lysosomal exocytosis leading to cellular clearance. This approach is particularly attractive in glycogen storage disease type II...

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Detalles Bibliográficos
Autores principales:	Spampanato, Carmine, Feeney, Erin, Li, Lishu, Cardone, Monica, Lim, Jeong-A, Annunziata, Fabio, Zare, Hossein, Polishchuk, Roman, Puertollano, Rosa, Parenti, Giancarlo, Ballabio, Andrea, Raben, Nina
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	WILEY-VCH Verlag 2013
Materias:	Research Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3662313/ https://www.ncbi.nlm.nih.gov/pubmed/23606558 http://dx.doi.org/10.1002/emmm.201202176

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