Cargando…
Development of gene therapy: potential in severe combined immunodeficiency due to adenosine deaminase deficiency
The history of stem cell gene therapy is strongly linked to the development of gene therapy for severe combined immunodeficiencies (SCID) and especially adenosine deaminase (ADA)-deficient SCID. Here we discuss the developments achieved in over two decades of clinical and laboratory research that le...
Autores principales: | Montiel-Equihua, Claudia A, Thrasher, Adrian J, Gaspar, H Bobby |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Dove Medical Press
2009
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3781725/ https://www.ncbi.nlm.nih.gov/pubmed/24198507 |
Ejemplares similares
-
Adenosine Deaminase Deficiency – More Than Just an Immunodeficiency
por: Whitmore, Kathryn V., et al.
Publicado: (2016) -
Review of Treatment for Adenosine Deaminase Deficiency (ADA) Severe Combined Immunodeficiency (SCID)
por: Secord, Elizabeth, et al.
Publicado: (2022) -
Combined Immunodeficiency Disease and Adenosine Deaminase Deficiency. A Molecular Defect
por: Baumgarten, Alexander
Publicado: (1976) -
First Occurrence of Plasmablastic Lymphoma in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Disease Patient and Review of the Literature
por: Migliavacca, Maddalena, et al.
Publicado: (2018) -
Atypical Omenn Syndrome due to Adenosine Deaminase Deficiency
por: Joshi, Avni Y., et al.
Publicado: (2012)