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Long-term effects of tafamidis for the treatment of transthyretin familial amyloid polyneuropathy

Tafamidis, a transthyretin (TTR) kinetic stabilizer, delayed neuropathic progression in patients with Val30Met TTR familial amyloid polyneuropathy (TTR-FAP) in an 18-month randomized controlled trial (study Fx-005). This 12-month, open-label extension study evaluated the long-term safety, tolerabili...

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Detalles Bibliográficos
Autores principales:	Coelho, Teresa, Maia, Luis F., da Silva, Ana Martins, Cruz, Márcia W., Planté-Bordeneuve, Violaine, Suhr, Ole B., Conceiçao, Isabel, Schmidt, Hartmut H.-J., Trigo, Pedro, Kelly, Jeffery W., Labaudinière, Richard, Chan, Jason, Packman, Jeff, Grogan, Donna R.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Springer Berlin Heidelberg 2013
Materias:	Original Communication
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3825212/ https://www.ncbi.nlm.nih.gov/pubmed/23974642 http://dx.doi.org/10.1007/s00415-013-7051-7

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