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Oligonucleotide-Based Therapy for FTD/ALS Caused by the C9orf72 Repeat Expansion: A Perspective

Amyotrophic lateral sclerosis (ALS) is a progressive and lethal disease of motor neuron degeneration, leading to paralysis of voluntary muscles and death by respiratory failure within five years of onset. Frontotemporal dementia (FTD) is characterised by degeneration of frontal and temporal lobes, l...

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Detalles Bibliográficos
Autores principales:	Fernandes, Stephanie A., Douglas, Andrew G. L., Varela, Miguel A., Wood, Matthew J. A., Aoki, Yoshitsugu
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Hindawi Publishing Corporation 2013
Materias:	Review Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3855979/ https://www.ncbi.nlm.nih.gov/pubmed/24349764 http://dx.doi.org/10.1155/2013/208245

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