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Accelerating development, registration and access to medicines for rare diseases in the European Union through adaptive approaches: features and perspectives

There is growing recognition that the current research-and-development (R&D) and innovation-regulation ecosystem could be made more efficient to stimulate and support access to innovative therapies for those patients with rare, life-threatening diseases for which there are no adequate licensed t...

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Detalles Bibliográficos
Autores principales:	Uguen, David, Lönngren, Thomas, Le Cam, Yann, Garner, Sarah, Voisin, Emmanuelle, Incerti, Carlo, Dunoyer, Marc, Slaoui, Moncef
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2014
Materias:	Letter to the Editor
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC3923002/ https://www.ncbi.nlm.nih.gov/pubmed/24513034 http://dx.doi.org/10.1186/1750-1172-9-20

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