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Evaluation of Retinoids for Induction of the Redundant Gene ABCD2 as an Alternative Treatment Option in X-Linked Adrenoleukodystrophy

X-linked adrenoleukodystrophy (X-ALD), the most common peroxisomal disorder, is a clinically heterogeneous disease that can manifest as devastating inflammatory cerebral demyelination (CALD) leading to death of affected males. Currently, the only curative treatment is allogeneic hematopoietic stem c...

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Detalles Bibliográficos
Autores principales:	Weber, Franziska D., Weinhofer, Isabelle, Einwich, Angelika, Forss-Petter, Sonja, Muneer, Zahid, Maier, Harald, Weber, Willi H. A., Berger, Johannes
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Public Library of Science 2014
Materias:	Research Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4117577/ https://www.ncbi.nlm.nih.gov/pubmed/25079382 http://dx.doi.org/10.1371/journal.pone.0103742

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