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Quality of Life is Improved and Kidney Function Preserved in Patients with Nephropathic Cystinosis Treated for 2 Years with Delayed-Release Cysteamine Bitartrate

OBJECTIVES: To determine the long-term effects of delayed-release cysteamine bitartrate (DR-CYS) based on our previous work that established the short-term noninferiority of DR-CYS every 12 hours compared with immediate-release cysteamine bitartrate every 6 hours. STUDY DESIGN: We conducted a prospe...

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Detalles Bibliográficos
Autores principales:	Langman, Craig B., Greenbaum, Larry A., Grimm, Paul, Sarwal, Minnie, Niaudet, Patrick, Deschenes, Georges, Cornelissen, Elisabeth A. M., Morin, Denis, Cochat, Pierre, Elenberg, Ewa, Hanna, Christian, Gaillard, Segolene, Bagger, Mary Jo, Rioux, Patrice
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	2014
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4181581/ https://www.ncbi.nlm.nih.gov/pubmed/24948347 http://dx.doi.org/10.1016/j.jpeds.2014.05.013

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