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Sanfilippo syndrome registry project and natural history studies: an example of patients, parents and researchers collaborating for a cure

Detalles Bibliográficos
Autores principales:	Wood, Jill, Siedman, Stuart, Siedman, Jennifer, Levy, Paul, Brown, Kyle, McBride, Kim, Flanigan, Kevin, Marques, Raquel, Feldman, Arleta, PleHcha, Robert, Ekins, Sean
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2014
Materias:	Poster Presentation
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4249675/ http://dx.doi.org/10.1186/1750-1172-9-S1-P7

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