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A Phase 2 Multi-center, Open-label, Switch-over Trial to Evaluate the Safety and Efficacy of Abcertin® in Patients with Type 1 Gaucher Disease

Gaucher disease is a lysosomal storage disease for which enzyme replacement therapy has proven to be effective. A switch-over clinical trial was performed to evaluate the efficacy and safety of Abcertin® (ISU Abxis, Seoul, Korea) in subjects with type 1 Gaucher disease who were previously treated wi...

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Detalles Bibliográficos
Autores principales:	Choi, Jin-Ho, Lee, Beom Hee, Ko, Jung Min, Sohn, Young Bae, Lee, Jin-Sung, Kim, Gu-Hwan, Heo, Sun Hee, Park, June-Young, Kim, Yoo-Mi, Kim, Ja-Hye, Yoo, Han-Wook
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	The Korean Academy of Medical Sciences 2015
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4366957/ https://www.ncbi.nlm.nih.gov/pubmed/25829804 http://dx.doi.org/10.3346/jkms.2015.30.4.378

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