Positive effect of erythrocyte-delivered dexamethasone in ataxia-telangiectasia

OBJECTIVE: Ataxia-telangiectasia (AT) is a rare, devastating neurodegenerative disease presenting with early-onset ataxia, oculocutaneous telangiectasia, immunodeficiency, radiosensitivity, and proneness to cancer. In a previous phase 2 study, we showed that 6 monthly infusions of autologous erythro...

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Detalles Bibliográficos
Autores principales: Leuzzi, Vincenzo, Micheli, Roberto, D'Agnano, Daniela, Molinaro, Anna, Venturi, Tullia, Plebani, Alessandro, Soresina, Annarosa, Marini, Mirella, Ferremi Leali, Pierino, Quinti, Isabella, Pietrogrande, Maria C., Finocchi, Andrea, Fazzi, Elisa, Chessa, Luciana, Magnani, Mauro
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Lippincott Williams & Wilkins 2015
Materias:
Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4396528/
https://www.ncbi.nlm.nih.gov/pubmed/25884015
http://dx.doi.org/10.1212/NXI.0000000000000098

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4396528/
https://www.ncbi.nlm.nih.gov/pubmed/25884015
http://dx.doi.org/10.1212/NXI.0000000000000098

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