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Increased Longevity and Metabolic Correction Following Syngeneic Bone Marrow Transplantation in a Murine Model of Mucopolysaccharidosis Type I

Mucopolysaccharidosis type I (MPS I) is an autosomal recessive inherited disease caused by deficiency of the glycosidase α-L-iduronidase (IDUA). Deficiency of IDUA leads to lysosomal accumulation of the glycosaminoglycans (GAG) heparan and dermatan sulfate and associated multi-systemic disease, the...

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Detalles Bibliográficos
Autores principales:	Wolf, Daniel A., Lenander, Andrew W., Nan, Zhenhong, Braunlin, Elizabeth A., Podetz-Pedersen, Kelly M., Whitley, Chester B., Gupta, Pankaj, Low, Walter C., McIvor, R. Scott
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	2011
Materias:	Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4465813/ https://www.ncbi.nlm.nih.gov/pubmed/22179554 http://dx.doi.org/10.1038/bmt.2011.239

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