Data from subjects receiving intrathecal laronidase for cervical spinal stenosis due to mucopolysaccharidosis type I

Five subjects with mucopolysaccharidosis type I and symptomatic cervical spinal stenosis received intrathecal laronidase in a 4-month pilot study and/or a 12-month extension study [1]. Clinical descriptions of study subjects, nonserious adverse events, individual data tables, and scoring system meth...

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Detalles Bibliográficos
Autores principales: Dickson, P.I., Kaitila, I., Harmatz, P., Mlikotic, A., Chen, A.H., Victoroff, A., Passage, M.B., Madden, J., Le, S.Q., Naylor, D.E.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2015
Materias:
Data Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4573094/
https://www.ncbi.nlm.nih.gov/pubmed/26484358
http://dx.doi.org/10.1016/j.dib.2015.08.004

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