Cargando…
Improving translational studies: lessons from rare neuromuscular diseases
Animal models play a key role in the development of novel treatments for human disease. This is particularly true for rare diseases – defined as disorders that affect less than 1 in 2000 people in the human population – for which, very often, there are no effective methods of treatment. Pharmaceutic...
Autor principal: | Wells, Dominic |
---|---|
Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
The Company of Biologists
2015
|
Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4610241/ https://www.ncbi.nlm.nih.gov/pubmed/26438690 http://dx.doi.org/10.1242/dmm.022616 |
Ejemplares similares
-
Establishing prevalence in rare neuromuscular diseases: A lesson from congenital myopathies
por: Bamaga, Ahmed K., et al.
Publicado: (2017) -
Improving translatability of preclinical studies for neuromuscular disorders: lessons from the TREAT-NMD Advisory Committee for Therapeutics (TACT)
por: Willmann, Raffaella, et al.
Publicado: (2020) -
The predictive value of models of neuromuscular disorders to potentiate clinical translation
por: van Putten, Maaike
Publicado: (2022) -
Lessons Learned From Translational Research in Neuromuscular Diseases: Impact on Study Design, Outcome Measures and Managing Expectation
por: Stimpson, Georgia, et al.
Publicado: (2021) -
Lessons learned from the pandemic that can be translated in the future
por: Ducharme, Anique
Publicado: (2022)