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A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy

A novel canine muscular dystrophy in Landseer dogs was observed. We had access to five affected dogs from two litters. The clinical signs started at a few weeks of age, and the severe progressive muscle weakness led to euthanasia between 5 and 15 months of age. The pedigrees of the affected dogs sug...

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Autores principales: Steffen, Frank, Bilzer, Thomas, Brands, Jan, Golini, Lorenzo, Jagannathan, Vidhya, Wiedmer, Michaela, Drögemüller, Michaela, Drögemüller, Cord, Leeb, Tosso
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Genetics Society of America 2015
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4683634/
https://www.ncbi.nlm.nih.gov/pubmed/26438297
http://dx.doi.org/10.1534/g3.115.021923
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author Steffen, Frank
Bilzer, Thomas
Brands, Jan
Golini, Lorenzo
Jagannathan, Vidhya
Wiedmer, Michaela
Drögemüller, Michaela
Drögemüller, Cord
Leeb, Tosso
author_facet Steffen, Frank
Bilzer, Thomas
Brands, Jan
Golini, Lorenzo
Jagannathan, Vidhya
Wiedmer, Michaela
Drögemüller, Michaela
Drögemüller, Cord
Leeb, Tosso
author_sort Steffen, Frank
collection PubMed
description A novel canine muscular dystrophy in Landseer dogs was observed. We had access to five affected dogs from two litters. The clinical signs started at a few weeks of age, and the severe progressive muscle weakness led to euthanasia between 5 and 15 months of age. The pedigrees of the affected dogs suggested a monogenic autosomal-recessive inheritance of the trait. Linkage and homozygosity mapping indicated two potential genome segments for the causative variant on chromosomes 10 and 31 harboring a total of 4.8 Mb of DNA or 0.2% of the canine genome. Using the Illumina sequencing technology, we obtained a whole-genome sequence from one affected Landseer. Variants were called with respect to the dog reference genome and compared with the genetic variants of 170 control dogs from other breeds. The affected Landseer dog was homozygous for a single, private nonsynonymous variant in the critical intervals, a nonsense variant in the COL6A1 gene (Chr31:39,303,964G>T; COL6A1:c.289G>T; p.E97*). Genotypes at this variant showed perfect concordance with the muscular dystrophy phenotype in all five cases and more than 1000 control dogs. Variants in the human COL6A1 gene cause Bethlem myopathy or Ullrich congenital muscular dystrophy. We therefore conclude that the identified canine COL6A1 variant is most likely causative for the observed muscular dystrophy in Landseer dogs. On the basis of the nature of the genetic variant in Landseer dogs and their severe clinical phenotype these dogs represent a model for human Ullrich congenital muscular dystrophy.
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spelling pubmed-46836342015-12-18 A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy Steffen, Frank Bilzer, Thomas Brands, Jan Golini, Lorenzo Jagannathan, Vidhya Wiedmer, Michaela Drögemüller, Michaela Drögemüller, Cord Leeb, Tosso G3 (Bethesda) Investigations A novel canine muscular dystrophy in Landseer dogs was observed. We had access to five affected dogs from two litters. The clinical signs started at a few weeks of age, and the severe progressive muscle weakness led to euthanasia between 5 and 15 months of age. The pedigrees of the affected dogs suggested a monogenic autosomal-recessive inheritance of the trait. Linkage and homozygosity mapping indicated two potential genome segments for the causative variant on chromosomes 10 and 31 harboring a total of 4.8 Mb of DNA or 0.2% of the canine genome. Using the Illumina sequencing technology, we obtained a whole-genome sequence from one affected Landseer. Variants were called with respect to the dog reference genome and compared with the genetic variants of 170 control dogs from other breeds. The affected Landseer dog was homozygous for a single, private nonsynonymous variant in the critical intervals, a nonsense variant in the COL6A1 gene (Chr31:39,303,964G>T; COL6A1:c.289G>T; p.E97*). Genotypes at this variant showed perfect concordance with the muscular dystrophy phenotype in all five cases and more than 1000 control dogs. Variants in the human COL6A1 gene cause Bethlem myopathy or Ullrich congenital muscular dystrophy. We therefore conclude that the identified canine COL6A1 variant is most likely causative for the observed muscular dystrophy in Landseer dogs. On the basis of the nature of the genetic variant in Landseer dogs and their severe clinical phenotype these dogs represent a model for human Ullrich congenital muscular dystrophy. Genetics Society of America 2015-10-01 /pmc/articles/PMC4683634/ /pubmed/26438297 http://dx.doi.org/10.1534/g3.115.021923 Text en Copyright © 2015 Steffen et al. http://creativecommons.org/licenses/by/4.0/ This is an open-access article distributed under the terms of the Creative Commons Attribution 4.0 International License (http://creativecommons.org/licenses/by/4.0/), which permits unrestricted use, distribution, and reproduction in any medium, provided the original work is properly cited.
spellingShingle Investigations
Steffen, Frank
Bilzer, Thomas
Brands, Jan
Golini, Lorenzo
Jagannathan, Vidhya
Wiedmer, Michaela
Drögemüller, Michaela
Drögemüller, Cord
Leeb, Tosso
A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy
title A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy
title_full A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy
title_fullStr A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy
title_full_unstemmed A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy
title_short A Nonsense Variant in COL6A1 in Landseer Dogs with Muscular Dystrophy
title_sort nonsense variant in col6a1 in landseer dogs with muscular dystrophy
topic Investigations
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4683634/
https://www.ncbi.nlm.nih.gov/pubmed/26438297
http://dx.doi.org/10.1534/g3.115.021923
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