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Profile of eliglustat tartrate in the management of Gaucher disease

Gaucher disease (GD) is a lysosomal storage disorder caused by the deficient activity of acid beta glucosidase, with consequent accumulation of glucosylceramide in the spleen, liver, bone marrow, and various organs and tissues. Currently, the gold standard for GD treatment is enzyme replacement ther...

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Detalles Bibliográficos
Autores principales:	Sechi, Annalisa, Dardis, Andrea, Bembi, Bruno
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Dove Medical Press 2016
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4714736/ https://www.ncbi.nlm.nih.gov/pubmed/26811686 http://dx.doi.org/10.2147/TCRM.S73226

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