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Sixty years of transthyretin familial amyloid polyneuropathy (TTR-FAP) in Europe: where are we now? A European network approach to defining the epidemiology and management patterns for TTR-FAP

PURPOSE OF REVIEW: Transthyretin familial amyloid polyneuropathy (TTR-FAP) is a highly disabling, life-threatening disease characterized by progressive sensorimotor and autonomic neuropathy. The profile of the disease across Europe is inadequately understood at present. RECENT FINDINGS: The incidenc...

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Detalles Bibliográficos
Autores principales:	Parman, Yesim, Adams, David, Obici, Laura, Galán, Lucía, Guergueltcheva, Velina, Suhr, Ole B., Coelho, Teresa
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Lippincott Williams & Wilkins 2016
Materias:	Supplement Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4739317/ https://www.ncbi.nlm.nih.gov/pubmed/26734951 http://dx.doi.org/10.1097/WCO.0000000000000288

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