Cargando…
Robust method for TALEN-edited correction of pF508del in patient-specific induced pluripotent stem cells
Cystic fibrosis is one of the most frequent inherited rare diseases, caused by mutations in the cystic fibrosis transmembrane conductance regulator gene. Apart from symptomatic treatments, therapeutic protocols for curing the disease have not yet been established. The regeneration of genetically cor...
| Autores principales: | , |
|---|---|
| Formato: | Online Artículo Texto |
| Lenguaje: | English |
| Publicado: |
BioMed Central
2016
|
| Materias: | |
| Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4748475/ https://www.ncbi.nlm.nih.gov/pubmed/26861665 http://dx.doi.org/10.1186/s13287-016-0275-6 |