Gene Therapy Corrects Mitochondrial Dysfunction in Hematopoietic Progenitor Cells and Fibroblasts from Coq9(R239X) Mice

Recent clinical trials have shown that in vivo and ex vivo gene therapy strategies can be an option for the treatment of several neurological disorders. Both strategies require efficient and safe vectors to 1) deliver the therapeutic gene directly into the CNS or 2) to genetically modify stem cells...

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Detalles Bibliográficos
Autores principales: Barriocanal-Casado, Eliana, Cueto-Ureña, Cristina, Benabdellah, Karim, Gutiérrez-Guerrero, Alejandra, Cobo, Marién, Hidalgo-Gutiérrez, Agustín, Rodríguez-Sevilla, Juan José, Martín, Francisco, López, Luis C.
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Public Library of Science 2016
Materias:
Research Article
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4920430/
https://www.ncbi.nlm.nih.gov/pubmed/27341668
http://dx.doi.org/10.1371/journal.pone.0158344

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