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Musculoskeletal manifestations in mucopolysaccharidosis type I (Hurler syndrome) following hematopoietic stem cell transplantation

BACKGROUND: Hematopoietic stem cell transplantation (HSCT) is the treatment of choice for young Hurler patients. Despite halting of neurocognitive decline and improvement of life expectancy, the beneficial effect on the skeletal system is limited. As orthopedic complications are one of the most disa...

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Detalles Bibliográficos
Autores principales:	Schmidt, Mona, Breyer, Sandra, Löbel, Ulrike, Yarar, Sinef, Stücker, Ralf, Ullrich, Kurt, Müller, Ingo, Muschol, Nicole
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	BioMed Central 2016
Materias:	Research
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4938899/ https://www.ncbi.nlm.nih.gov/pubmed/27392569 http://dx.doi.org/10.1186/s13023-016-0470-7

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