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Clinical trial network for the promotion of clinical research for rare diseases in Japan: muscular dystrophy clinical trial network
BACKGROUND: Duchenne muscular dystrophy (DMD) is the most commonly inherited neuromuscular disease. Therapeutic agents for the treatment of rare disease, namely “orphan drugs”, have recently drawn the attention of researchers and pharmaceutical companies. To ensure the successful conduction of clini...
Autores principales: | Shimizu, Reiko, Ogata, Katsuhisa, Tamaura, Akemi, Kimura, En, Ohata, Maki, Takeshita, Eri, Nakamura, Harumasa, Takeda, Shin’ichi, Komaki, Hirofumi |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BioMed Central
2016
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4939632/ https://www.ncbi.nlm.nih.gov/pubmed/27401940 http://dx.doi.org/10.1186/s12913-016-1477-4 |
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