Cargando…

Health‐related quality of life in patients with Duchenne muscular dystrophy: a multinational, cross‐sectional study

AIM: To estimate health‐related quality of life (HRQOL) in patients with Duchenne muscular dystrophy (DMD). METHOD: HRQOL was assessed using the Health Utilities Index Questionnaire (HUI) and the Pediatric Quality of Life Inventory (PedsQL) neuromuscular module version 3.0 online. Results were strat...

Descripción completa

Detalles Bibliográficos
Autores principales:	Landfeldt, Erik, Lindgren, Peter, Bell, Christopher F, Guglieri, Michela, Straub, Volker, Lochmüller, Hanns, Bushby, Katharine
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2015
Materias:	Original Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4949722/ https://www.ncbi.nlm.nih.gov/pubmed/26483095 http://dx.doi.org/10.1111/dmcn.12938

Ejemplares similares

Quantifying the burden of caregiving in Duchenne muscular dystrophy
por: Landfeldt, Erik, et al.
Publicado: (2016)

The burden of Duchenne muscular dystrophy: An international, cross-sectional study
por: Landfeldt, Erik, et al.
Publicado: (2014)

Compliance to Care Guidelines for Duchenne Muscular Dystrophy
por: Landfeldt, Erik, et al.
Publicado: (2015)

Economic Evaluation in Duchenne Muscular Dystrophy: Model Frameworks for Cost-Effectiveness Analysis
por: Landfeldt, Erik, et al.
Publicado: (2016)

Incomplete description of the current body of evidence of the health economics of Duchenne muscular dystrophy
por: Landfeldt, Erik, et al.
Publicado: (2019)

Improving recognition of Duchenne muscular dystrophy: a retrospective case note review
por: van Ruiten, Henriette J A, et al.
Publicado: (2014)

Life expectancy at birth in Duchenne muscular dystrophy: a systematic review and meta-analysis
por: Landfeldt, Erik, et al.
Publicado: (2020)

Adult care for Duchenne muscular dystrophy in the UK
por: Rodger, Sunil, et al.
Publicado: (2014)

Muscle-Derived Proteins as Serum Biomarkers for Monitoring Disease Progression in Three Forms of Muscular Dystrophy
por: Burch, Peter M., et al.
Publicado: (2015)

Extending Life in Duchenne Muscular Dystrophy: Implications for Appraisals of Cost-Effectiveness
por: Landfeldt, Erik
Publicado: (2018)

Gene therapy in Duchenne muscular dystrophy: Identifying and preparing for the challenges ahead
por: Heslop, Emma, et al.
Publicado: (2021)

The impact of testosterone therapy on quality of life in adolescents with Duchenne muscular dystrophy
por: Wood, CL, et al.
Publicado: (2021)

Dystromirs as Serum Biomarkers for Monitoring the Disease Severity in Duchenne Muscular Dystrophy
por: Zaharieva, Irina T., et al.
Publicado: (2013)

An update on Becker muscular dystrophy
por: Straub, Volker, et al.
Publicado: (2023)

Transition from childhood to adulthood in Duchenne muscular dystrophy (DMD)
por: Rodger, Sunil, et al.
Publicado: (2012)

MON-LB050 Preliminary Results from the "Observational Study of Clinical Outcomes for Testosterone Treatment of Pubertal Delay in Duchenne Muscular Dystrophy (DMD) (NCT 02571205)"
por: Wood, Claire, et al.
Publicado: (2019)

Is ongoing testosterone required after pubertal induction in Duchenne muscular dystrophy?
por: Wood, Claire L, et al.
Publicado: (2023)

Life Expectancy in Duchenne Muscular Dystrophy: Reproduced Individual Patient Data Meta-analysis
por: Broomfield, Jonathan, et al.
Publicado: (2021)

Increased dystrophin production with golodirsen in patients with Duchenne muscular dystrophy
por: Frank, Diane E., et al.
Publicado: (2020)

Quantitative Magnetic Resonance Imaging in Limb-Girdle Muscular Dystrophy 2I: A Multinational Cross-Sectional Study
por: Willis, Tracey A., et al.
Publicado: (2014)

The importance of genetic diagnosis for Duchenne muscular dystrophy
por: Aartsma-Rus, Annemieke, et al.
Publicado: (2016)

Tracking disease progression non‐invasively in Duchenne and Becker muscular dystrophies
por: Spitali, Pietro, et al.
Publicado: (2018)

New aspects on patients affected by dysferlin deficient muscular dystrophy
por: Klinge, Lars, et al.
Publicado: (2009)

Longitudinal serum biomarker screening identifies malate dehydrogenase 2 as candidate prognostic biomarker for Duchenne muscular dystrophy
por: Signorelli, Mirko, et al.
Publicado: (2019)

Respiratory involvement in ambulant and non-ambulant patients with facioscapulohumeral muscular dystrophy
por: Moreira, Sandra, et al.
Publicado: (2017)

Comparative proteomic analyses of Duchenne muscular dystrophy and Becker muscular dystrophy muscles: changes contributing to preserve muscle function in Becker muscular dystrophy patients
por: Capitanio, Daniele, et al.
Publicado: (2020)

Attenuated muscle regeneration is a key factor in dysferlin-deficient muscular dystrophy
por: Chiu, Yen-Hui, et al.
Publicado: (2009)

Development of a New Quality of Life Measure for Duchenne Muscular Dystrophy Using Mixed Methods: The DMD-QoL
por: Powell, Philip A., et al.
Publicado: (2021)

Observational study of clinical outcomes for testosterone treatment of pubertal delay in Duchenne muscular dystrophy
por: Wood, C. L., et al.
Publicado: (2019)

Blood-derived biomarkers correlate with clinical progression in Duchenne muscular dystrophy
por: Strandberg, Kristin, et al.
Publicado: (2020)

Neurocognitive Profiles in Duchenne Muscular Dystrophy and Gene Mutation Site
por: D’Angelo, Maria Grazia, et al.
Publicado: (2011)

Imperatives for DUCHENNE MD: a Simplified Guide to Comprehensive Care for Duchenne Muscular Dystrophy
por: Kinnett, Kathi, et al.
Publicado: (2015)

The administration of antisense oligonucleotide golodirsen reduces pathological regeneration in patients with Duchenne muscular dystrophy
por: Scaglioni, Dominic, et al.
Publicado: (2021)

Validation of genetic modifiers for Duchenne muscular dystrophy: a multicentre study assessing SPP1 and LTBP4 variants
por: van den Bergen, Janneke C, et al.
Publicado: (2015)

Measurement of salivary testosterone in adolescents and young men with Duchenne muscular dystrophy
por: Sahun, Yolanda Alins, et al.
Publicado: (2021)

Prognostic indicators of disease progression in Duchenne muscular dystrophy: A literature review and evidence synthesis
por: Ferizovic, Nermina, et al.
Publicado: (2022)

Health-Related Quality of Life in Patients with Adult-Onset Myotonic Dystrophy Type 1: A Systematic Review
por: Landfeldt, Erik, et al.
Publicado: (2019)

European Cross-Sectional Survey of Current Care Practices for Duchenne Muscular Dystrophy Reveals Regional and Age-Dependent Differences
por: Vry, Julia, et al.
Publicado: (2016)

Decoding the transcriptome of Duchenne muscular dystrophy to the single nuclei level reveals clinical-genetic correlations
por: Suárez-Calvet, Xavier, et al.
Publicado: (2023)

Costs of Illness of Spinal Muscular Atrophy: A Systematic Review
por: Landfeldt, Erik, et al.
Publicado: (2021)

Cannot write session to /tmp/vufind_sessions/sess_eopkts4i974os44ts2pvntkuq3