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A systematic review to investigate the measurement properties of goal attainment scaling, towards use in drug trials
BACKGROUND: One of the main challenges for drug evaluation in rare diseases is the often heterogeneous course of these diseases. Traditional outcome measures may not be applicable for all patients, when they are in different stages of their disease. For instance, in Duchenne Muscular Dystrophy, the...
Autores principales: | Gaasterland, Charlotte M. W., Jansen-van der Weide, Marijke C., Weinreich, Stephanie S., van der Lee, Johanna H. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BioMed Central
2016
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC4989379/ https://www.ncbi.nlm.nih.gov/pubmed/27534620 http://dx.doi.org/10.1186/s12874-016-0205-4 |
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