Hematopoietic Stem cell transplantation and lentiviral vector‐based gene therapy for Krabbe's disease: Present convictions and future prospects

Currently, presymtomatic hematopoietic stem and progenitor cell transplantation (HSPCT) is the only therapeutic modality that alleviates Krabbe's disease (KD)‐induced central nervous system damage. However, all HSPCT‐treated patients exhibit severe deterioration in peripheral nervous system fun...

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Detalles Bibliográficos
Autores principales: Hu, Peirong, Li, Yedda, Nikolaishvili‐Feinberg, Nana, Scesa, Giuseppe, Bi, Yanmin, Pan, Dao, Moore, Dominic, Bongarzone, Ernesto R., Sands, Mark S., Miller, Ryan, Kafri, Tal
Formato: Online Artículo Texto
Lenguaje:English
Publicado: John Wiley and Sons Inc. 2016
Materias:
Therapies and Clinical Management
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5027985/
https://www.ncbi.nlm.nih.gov/pubmed/27638600
http://dx.doi.org/10.1002/jnr.23847

Internet

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5027985/
https://www.ncbi.nlm.nih.gov/pubmed/27638600
http://dx.doi.org/10.1002/jnr.23847

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