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Seven‐year safety and efficacy with velaglucerase alfa for treatment‐naïve adult patients with type 1 Gaucher disease

Velaglucerase alfa is a human β‐glucocerebrosidase approved for Gaucher disease type 1 (GD1) treatment. This report summarizes the 7‐year experience of the now‐completed phase I/II and extension studies of adult GD1 patients who received velaglucerase alfa. Ten patients who completed the 9‐month, ph...

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Detalles Bibliográficos
Autores principales:	Zimran, Ari, Wang, Nan, Ogg, Carol, Crombez, Eric, Cohn, Gabriel M., Elstein, Deborah
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	John Wiley and Sons Inc. 2015
Materias:	Original Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5033020/ https://www.ncbi.nlm.nih.gov/pubmed/25903392 http://dx.doi.org/10.1002/ajh.24040

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