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Gene therapy for metabolic diseases
Gene therapy has recently shown great promise as an effective treatment for a number of metabolic diseases caused by genetic defects in both animal models and human clinical trials. Most of the current success has been achieved using a viral mediated gene addition approach, but gene-editing technolo...
Autores principales: | Chandler, Randy J., Venditti, Charles P. |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
IOS Press
2016
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5108627/ https://www.ncbi.nlm.nih.gov/pubmed/27853673 http://dx.doi.org/10.3233/TRD-160007 |
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