Cargando…

Adeno-Associated Virus Gene Therapy for Liver Disease

The field of adeno-associated virus (AAV) gene therapy has progressed rapidly over the past decade, with the advent of novel capsid serotype and organ-specific promoters, and an increasing understanding of the immune response to AAV administration. In particular, liver-directed therapy has made rema...

Descripción completa

Detalles Bibliográficos
Autores principales:	Kattenhorn, Lisa M., Tipper, Christopher H., Stoica, Lorelei, Geraghty, Deborah S., Wright, Teresa L., Clark, K. Reed, Wadsworth, Samuel C.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Mary Ann Liebert, Inc. 2016
Materias:	Review Articles
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5177998/ https://www.ncbi.nlm.nih.gov/pubmed/27897038 http://dx.doi.org/10.1089/hum.2016.160

Ejemplares similares

Adeno Associated Viral Vector Delivered RNAi for Gene Therapy of SOD1 Amyotrophic Lateral Sclerosis
por: Stoica, Lorelei, et al.
Publicado: (2016)

Determining the Minimally Effective Dose of a Clinical Candidate Adeno-Associated Virus Vector in a Mouse Model of Hemophilia A
por: Greig, Jenny A., et al.
Publicado: (2022)

My Pathway to Adeno-Associated Virus and Adeno-Associated Virus Gene Therapy: A Personal Perspective
por: Carter, Barrie J.
Publicado: (2020)

Emerging therapeutic potential of adeno-associated virus-mediated gene therapy in liver fibrosis
por: Bu, Fang-tian, et al.
Publicado: (2022)

Adeno-Associated Virus-Based Gene Therapy for CNS Diseases
por: Hocquemiller, Michaël, et al.
Publicado: (2016)

Adeno-Associated Virus Mediated Gene Therapy for Corneal Diseases
por: Bastola, Prabhakar, et al.
Publicado: (2020)

Visualization of gene therapy with a liver cancer-targeted adeno-associated virus 3 vector
por: Liu, Xusheng, et al.
Publicado: (2020)

Modulation of the liver immune microenvironment by the adeno-associated virus serotype 8 gene therapy vector
por: Carestia, Agostina, et al.
Publicado: (2020)

Adeno‐associated virus serotype 2 capsid variants for improved liver‐directed gene therapy
por: Meumann, Nadja, et al.
Publicado: (2023)

Adeno-Associated Virus (AAV) as a Vector for Gene Therapy
por: Naso, Michael F., et al.
Publicado: (2017)

Adeno‐associated virus (AAV)-based gene therapy for glioblastoma
por: Xu, Xin, et al.
Publicado: (2021)

Simple Purification of Adeno-Associated Virus-DJ for Liver-Specific Gene Expression
por: Liu, Jingjing, et al.
Publicado: (2016)

Routes of administration for adeno-associated viruses carrying gene therapies for brain diseases
por: Zhou, Kai, et al.
Publicado: (2022)

Improved adeno-associated virus (AAV) serotype 1 and 5 vectors for gene therapy
por: Sen, Dwaipayan, et al.
Publicado: (2013)

The state of the art of adeno-associated virus-based vectors in gene therapy
por: Coura, Renata dos Santos, et al.
Publicado: (2007)

Characteristics and advantages of adeno-associated virus vector-mediated gene therapy for neurodegenerative diseases
por: Qu, Yuan, et al.
Publicado: (2019)

Adeno-Associated Virus (AAV) - Based Gene Therapies for Retinal Diseases: Where are We?
por: Ail, Divya, et al.
Publicado: (2023)

Correction: The state of the art of adeno-associated virus-based vectors in gene therapy
por: dos Santos Coura, Renata, et al.
Publicado: (2010)

Evaluation of Cellular Immune Response to Adeno-Associated Virus-Based Gene Therapy
por: Gorovits, Boris, et al.
Publicado: (2023)

Recombinant adeno-associated virus 8 vector in gene therapy: Opportunities and challenges
por: Zhao, Liyuan, et al.
Publicado: (2023)

Adeno-associated virus receptor complexes and implications for adeno-associated virus immune neutralization
por: Large, Edward E., et al.
Publicado: (2023)

Autophagy determines efficiency of liver‐directed gene therapy with adeno‐associated viral vectors
por: Hösel, Marianna, et al.
Publicado: (2017)

The Role of the Adeno-Associated Virus Capsid in Gene Transfer
por: Van Vliet, Kim M., et al.
Publicado: (2008)

Adeno‐associated virus‐vectored erythropoietin gene therapy for anemia in cats with chronic kidney disease
por: Vaden, Shelly L., et al.
Publicado: (2023)

The Platform Vector Gene Therapies Project: Increasing the Efficiency of Adeno-Associated Virus Gene Therapy Clinical Trial Startup
por: Brooks, Philip J., et al.
Publicado: (2020)

Ocular Gene Therapy with Adeno-associated Virus Vectors: Current Outlook for Patients and Researchers
por: Casey, Geoffrey A., et al.
Publicado: (2020)

Structure of the gene therapy vector, adeno-associated virus with its cell receptor, AAVR
por: Meyer, Nancy L, et al.
Publicado: (2019)

Emerging Immunogenicity and Genotoxicity Considerations of Adeno-Associated Virus Vector Gene Therapy for Hemophilia
por: Monahan, Paul E., et al.
Publicado: (2021)

Central nervous system-targeted adeno-associated virus gene therapy in methylmalonic acidemia
por: May, Francis J., et al.
Publicado: (2021)

Harnessing the Natural Biology of Adeno-Associated Virus to Enhance the Efficacy of Cancer Gene Therapy
por: Bower, Jacquelyn J., et al.
Publicado: (2021)

Recombinant Adeno-Associated Virus Serotype 9 Gene Therapy in Spinal Muscular Atrophy
por: Kotulska, Katarzyna, et al.
Publicado: (2021)

Rapid characterization of adeno-associated virus (AAV) gene therapy vectors by mass photometry
por: Wu, Di, et al.
Publicado: (2022)

Gene therapy of adeno‐associated virus (AAV) vectors in preclinical models of ischemic stroke
por: Wang, Jing, et al.
Publicado: (2023)

Seek and destroy: targeted adeno-associated viruses for gene delivery to hepatocellular carcinoma
por: Dhungel, Bijay, et al.
Publicado: (2017)

The SUMOylation Pathway Restricts Gene Transduction by Adeno-Associated Viruses
por: Hölscher, Christina, et al.
Publicado: (2015)

Different tropism of adenoviruses and adeno-associated viruses to corneal cells: implications for corneal gene therapy
por: Liu, J., et al.
Publicado: (2008)

Gene therapy of renal cancer using recombinant adeno-associated virus encoding human endostatin
por: Sun, Erlin, et al.
Publicado: (2018)

 Adeno-associated Virus (AAV) Dual Vector Strategies for Gene Therapy Encoding Large Transgenes
por: McClements, Michelle E., et al.
Publicado: (2017)

Enhancement of Adeno-Associated Virus-Mediated Gene Therapy Using Hydroxychloroquine in Murine and Human Tissues
por: Chandler, Laurel C., et al.
Publicado: (2019)

Adeno‐associated virus serotype 1‐based gene therapy for FTD caused by GRN mutations
por: Hinderer, Christian, et al.
Publicado: (2020)

Cannot write session to /tmp/vufind_sessions/sess_uhh00q2fqpl4ol374ctqtdoem0