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Follistatin Gene Therapy Improves Ambulation in Becker Muscular Dystrophy

Follistatin is a ubiquitous secretory propeptide that functions as a potent inhibitor of the myostatin pathway, resulting in an increase in skeletal muscle mass. Its ability to interact with the pituitary activin-inhibin axis and suppress the secretion of follicle-stimulating hormone (FSH) called fo...

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Detalles Bibliográficos
Autores principales:	Al-Zaidy, Samiah A., Sahenk, Zarife, Rodino-Klapac, Louise R., Kaspar, Brian, Mendell, Jerry R.
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	IOS Press 2015
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5240576/ https://www.ncbi.nlm.nih.gov/pubmed/27858738 http://dx.doi.org/10.3233/JND-150083

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