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Comparative study of idursulfase beta and idursulfase in vitro and in vivo

Hunter syndrome is an X-linked lysosomal storage disease caused by a deficiency in the enzyme iduronate-2-sulfatase (IDS), leading to the accumulation of glycosaminoglycans (GAGs). Two recombinant enzymes, idursulfase and idursulfase beta are currently available for enzyme replacement therapy for Hu...

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Detalles Bibliográficos
Autores principales:	Kim, Chihwa, Seo, Jinwook, Chung, Yokyung, Ji, Hyi-Jeong, Lee, Jaehyeon, Sohn, Jongmun, Lee, Byoungju, Jo, Eui-cheol
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Nature Publishing Group 2017
Materias:	Original Article
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5285491/ https://www.ncbi.nlm.nih.gov/pubmed/27829684 http://dx.doi.org/10.1038/jhg.2016.133

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