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Duchenne Regulatory Science Consortium Meeting on Disease Progression Modeling for Duchenne Muscular Dystrophy

Introduction: The Duchenne Regulatory Science Consortium (D-RSC) was established to develop tools to accelerate drug development for DMD. The resulting tools are anticipated to meet validity requirements outlined by qualification/endorsement pathways at both the U.S. Food and Drug Administration (F...

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Detalles Bibliográficos
Autores principales:	Larkindale, Jane, Abresch, Richard, Aviles, Enrique, Bronson, Abby, Chin, Janice, Furlong, Pat, Gordish-Dressman, Heather, Habeeb-Louks, Elizabeth, Henricson, Erik, Kroger, Hans, Lynn, Charles, Lynn, Stephen, Martin, Dana, Nuckolls, Glen, Rooney, William, Romero, Klaus, Sweeney, Lee, Vandenborne, Krista, Walter, Glenn, Wolff, Jodi, Wong, Brenda, McDonald, Craig M., Duchenne Regulatory Science Consortium, Imaging-DMD Consortium and the CINRG Investigators, members of the
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	Public Library of Science 2017
Materias:	Muscular Dystrophy
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5300692/ https://www.ncbi.nlm.nih.gov/pubmed/28228973 http://dx.doi.org/10.1371/currents.md.83071bbd728982f2f1073f4950e03586

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