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Gene therapy for primary immune deficiencies: a Canadian perspective
The use of gene therapy (GT) for the treatment of primary immune deficiencies (PID) including severe combined immune deficiency (SCID) has progressed significantly in the recent years. In particular, long-term studies have shown that adenosine deaminase (ADA) gene delivery into ADA-deficient hematop...
Autores principales: | Xu, Xiaobai, Tailor, Chetankumar S., Grunebaum, Eyal |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
BioMed Central
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5327566/ https://www.ncbi.nlm.nih.gov/pubmed/28261277 http://dx.doi.org/10.1186/s13223-017-0184-y |
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