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Viral Vector-Mediated Antisense Therapy for Genetic Diseases
RNA plays complex roles in normal health and disease and is becoming an important target for therapeutic intervention; accordingly, therapeutic strategies that modulate RNA function have gained great interest over the past decade. Antisense oligonucleotides (AOs) are perhaps the most promising strat...
Autores principales: | Imbert, Marine, Dias-Florencio, Gabriella, Goyenvalle, Aurélie |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
MDPI
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5333040/ https://www.ncbi.nlm.nih.gov/pubmed/28134780 http://dx.doi.org/10.3390/genes8020051 |
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