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The CRB1 Complex: Following the Trail of Crumbs to a Feasible Gene Therapy Strategy
Once considered science fiction, gene therapy is rapidly becoming scientific reality, targeting a growing number of the approximately 250 genes linked to hereditary retinal disorders such as retinitis pigmentosa and Leber's congenital amaurosis. Powerful new technologies have emerged, leading t...
Autores principales: | Quinn, Peter M., Pellissier, Lucie P., Wijnholds, Jan |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Frontiers Media S.A.
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5380682/ https://www.ncbi.nlm.nih.gov/pubmed/28424578 http://dx.doi.org/10.3389/fnins.2017.00175 |
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