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Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
Autores principales: | , , , |
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Formato: | Online Artículo Texto |
Lenguaje: | English |
Publicado: |
Elsevier
2017
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Materias: | |
Acceso en línea: | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5440743/ https://www.ncbi.nlm.nih.gov/pubmed/28560178 http://dx.doi.org/10.1016/j.ymgmr.2017.05.005 |
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author | Schänzer, Anne Giese, Kerstin Viergutz, Lara Hahn, Andreas |
author_facet | Schänzer, Anne Giese, Kerstin Viergutz, Lara Hahn, Andreas |
author_sort | Schänzer, Anne |
collection | PubMed |
description | |
format | Online Article Text |
id | pubmed-5440743 |
institution | National Center for Biotechnology Information |
language | English |
publishDate | 2017 |
publisher | Elsevier |
record_format | MEDLINE/PubMed |
spelling | pubmed-54407432017-05-30 Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. Schänzer, Anne Giese, Kerstin Viergutz, Lara Hahn, Andreas Mol Genet Metab Rep Correspondence Elsevier 2017-05-16 /pmc/articles/PMC5440743/ /pubmed/28560178 http://dx.doi.org/10.1016/j.ymgmr.2017.05.005 Text en © 2017 The Authors http://creativecommons.org/licenses/by-nc-nd/4.0/ This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/). |
spellingShingle | Correspondence Schänzer, Anne Giese, Kerstin Viergutz, Lara Hahn, Andreas Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. |
title | Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. |
title_full | Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. |
title_fullStr | Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. |
title_full_unstemmed | Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. |
title_short | Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. |
title_sort | letter to the editors: concerning “divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset pompe disease treated in the symptomatic or pre-symptomatic state” by takashi et al. and letter to the editors by ortolano et al. |
topic | Correspondence |
url | https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5440743/ https://www.ncbi.nlm.nih.gov/pubmed/28560178 http://dx.doi.org/10.1016/j.ymgmr.2017.05.005 |
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