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Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.

Detalles Bibliográficos
Autores principales: Schänzer, Anne, Giese, Kerstin, Viergutz, Lara, Hahn, Andreas
Formato: Online Artículo Texto
Lenguaje:English
Publicado: Elsevier 2017
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5440743/
https://www.ncbi.nlm.nih.gov/pubmed/28560178
http://dx.doi.org/10.1016/j.ymgmr.2017.05.005
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author Schänzer, Anne
Giese, Kerstin
Viergutz, Lara
Hahn, Andreas
author_facet Schänzer, Anne
Giese, Kerstin
Viergutz, Lara
Hahn, Andreas
author_sort Schänzer, Anne
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spelling pubmed-54407432017-05-30 Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al. Schänzer, Anne Giese, Kerstin Viergutz, Lara Hahn, Andreas Mol Genet Metab Rep Correspondence Elsevier 2017-05-16 /pmc/articles/PMC5440743/ /pubmed/28560178 http://dx.doi.org/10.1016/j.ymgmr.2017.05.005 Text en © 2017 The Authors http://creativecommons.org/licenses/by-nc-nd/4.0/ This is an open access article under the CC BY-NC-ND license (http://creativecommons.org/licenses/by-nc-nd/4.0/).
spellingShingle Correspondence
Schänzer, Anne
Giese, Kerstin
Viergutz, Lara
Hahn, Andreas
Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
title Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
title_full Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
title_fullStr Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
title_full_unstemmed Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
title_short Letter to the Editors: Concerning “Divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state” by Takashi et al. and Letter to the Editors by Ortolano et al.
title_sort letter to the editors: concerning “divergent clinical outcomes of alpha-glucosidase enzyme replacement therapy in two siblings with infantile-onset pompe disease treated in the symptomatic or pre-symptomatic state” by takashi et al. and letter to the editors by ortolano et al.
topic Correspondence
url https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5440743/
https://www.ncbi.nlm.nih.gov/pubmed/28560178
http://dx.doi.org/10.1016/j.ymgmr.2017.05.005
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