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Induced pluripotent stem cell models of lysosomal storage disorders

Induced pluripotent stem cells (iPSCs) have provided new opportunities to explore the cell biology and pathophysiology of human diseases, and the lysosomal storage disorder research community has been quick to adopt this technology. Patient-derived iPSC models have been generated for a number of lys...

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Detalles Bibliográficos
Autores principales:	Borger, Daniel K., McMahon, Benjamin, Roshan Lal, Tamanna, Serra-Vinardell, Jenny, Aflaki, Elma, Sidransky, Ellen
Formato:	Online Artículo Texto
Lenguaje:	English
Publicado:	The Company of Biologists Ltd 2017
Materias:	Review
Acceso en línea:	https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5483008/ https://www.ncbi.nlm.nih.gov/pubmed/28592657 http://dx.doi.org/10.1242/dmm.029009

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