Cargando…

Thermal Stability as a Determinant of AAV Serotype Identity

Currently, there are over 150 ongoing clinical trials utilizing adeno-associated viruses (AAVs) to target various genetic diseases, including hemophilia (AAV2 and AAV8), congenital heart failure (AAV1 and AAV6), cystic fibrosis (AAV2), rheumatoid arthritis (AAV2), and Batten disease (AAVrh.10). Prio...

Descripción completa

Detalles Bibliográficos
Autores principales: Bennett, Antonette, Patel, Saajan, Mietzsch, Mario, Jose, Ariana, Lins-Austin, Bridget, Yu, Jennifer C., Bothner, Brian, McKenna, Robert, Agbandje-McKenna, Mavis
Formato: Online Artículo Texto
Lenguaje:English
Publicado: American Society of Gene & Cell Therapy 2017
Materias:
Acceso en línea:https://www.ncbi.nlm.nih.gov/pmc/articles/PMC5552060/
https://www.ncbi.nlm.nih.gov/pubmed/28828392
http://dx.doi.org/10.1016/j.omtm.2017.07.003